Hoppe CC, Inati AC, Brown C, et al. Initial Results from a Cohort in a Phase 2a Study (GBT440-007) Evaluating Adolescents with Sickle Cell Disease Treated with Multiple Doses of GBT440, a HbS Polymerization Inhibitor. ASH 59th Annual Meeting & Exhibition, abstract 689.
Ongelijkheid in financiering van onderzoek naar sikkelcelziekte, cystische fibrose en hemofilie
nov 2025 | Benigne hematologie