Cappellini MD, Viprakasit V, Taher A, et al. The Believe trial: results of a phase 3, randomized, double-blind, placebo-controlled study of luspatercept in adult beta-thalassemia patients who require regular red blood cell (RBC) transfusions. ASH Annual Meeting and Exposition 2018, abstract 163.,Fenaux P, Platzbecker U, Mufti GJ, et al. The Medalist trial: results of a phase 3, randomized, double-blind, placebo-controlled study of luspatercept to treat anemia in patients with very low-, low-, or intermediate-risk myelodysplastic syndromes (MDS) with ring sideroblasts (RS) who require red blood cell (RBC) transfusions. ASH Annual Meeting and Exposition 2018, abstract 1.
Behandeling met emicizumab bij ernstige hemofilie alleen in basispakket na prijsdaling
feb 2020 | Benigne hematologie