“Toekomstige CF-patiënten kunnen misschien wel 80 jaar worden”

Bronnen:

1. 1. Keating D, Marigowda G, Burr, et al. VX-445-Tezacaftor-Ivacaftor in Patients with Cystic Fibrosis and One or Two Phe508del Alleles. N Engl J Med. 2018;379:1612-20.,2. Davies JC, Moskowitz SM, Brown C, et al. VX-659-Tezacaftor-Ivacaftor in Patients with Cystic Fibrosis and One or Two Phe508del Alleles. N Engl J Med. 2018;379:1599-611.