Adams D, Gonzalez-Duarte A, Patisiran, O'Riordan W, et al. an Investigational RNAi Therapeutic for Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Polyneuropathy: Results from the Phase 3 APOLLO study. AAN 2018, CT.001.
Gen-omgevingsinteracties bij ALS: rol van roken, alcohol, BMI en C9orf72-status
mei 2021 | Neuro-musculair